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New ruthenium compounds bearing semicarbazone 2-formylopyridine moiety: Playing with auxiliary ligands for tuning the mechanism of biological activity.

PMID: 28738277
Accepted Manuscript New ruthenium compounds bearing semicarbazone 2-formylopyridine moiety: Playing with auxiliary ligands for tuning the mechanism of biological activity Michał Łomzik, Olga Mazuryk, Dorota Rutkowska-Zbik, Grażyna Stochel, Philippe C. Gros, Małgorzata Brindell PII: DOI: Reference: S0162-0134(17)30314-8 doi: 10.1016/j.jinorgbio.2017.07.006 JIB 10253 To appear in: Journal of Inorganic Biochemistry Received date: Revised date: Accepted date: 3 May 2017 4 July 2017 9 July 2017 Please cite this article as: Michał Łomzik, Olga Mazuryk, Dorota Rutkowska-Zbik, Grażyna Stochel, Philippe C. Gros, Małgorzata Brindell , New ruthenium compounds bearing semicarbazone 2-formylopyridine moiety: Playing with auxiliary ligands for tuning the mechanism of biological activity, Journal of Inorganic Biochemistry (2017), doi: 10.1016/j.jinorgbio.2017.07.006 This is a PDF file of an unedited manuscript that has been accepted for publication. As a service to our customers we are providing this early version of the manuscript. The manuscript will undergo copyediting, typesetting, and review of the resulting proof before it is published in its final form. Please note that during the production process errors may be discovered which could affect the content, and all legal disclaimers that apply to the journal pertain. ACCEPTED MANUSCRIPT New Ruthenium Compounds bearing Semicarbazone 2Formylopyridine Moiety: Playing with Auxiliary Ligands for Tuning the Mechanism of CR IP T Biological Activity US Michał Łomzik,#[a],[b] Olga Mazuryk,#[a] Dorota Rutkowska-Zbik,[c] Grażyna Stochel, [a] Philippe AN C. Gros,* [b] and Małgorzata Brindell*[a] M [a] Department of Inorganic Chemistry, Faculty of Chemistry, Jagiellonian University Ingardena ED 3, 30-060 Krakow, Poland. brindell@chemia.uj.edu.pl [b] Université de Lorraine, CNRS, UMR SRSMC, HecRIn, Boulevard des Aiguillettes PT Vandoeuvre-Lès-Nancy, France. philippe.gros@univ-lorraine.fr CE [c] Jerzy Haber Institute of Catalysis and Surface Chemistry, Polish Academy of Sciences, # AC Niezapominajek 8, 30-239 Krakow, Poland. both authors contributed equally to this work * corresponding authors: P.G. : email: philippe.gros@univ-lorraine.fr, phone: +33383684979 ; M. B. : email: brindell@chemia.uj.edu.pl, phone: +48126632221. Keywords ruthenium, polypyridine, semicarbazone, anticancer activity, apoptosis, auxiliary ligands 1 ACCEPTED MANUSCRIPT Abstract Two ruthenium(II) complexes Ru1 and Ru2 bearing as a one ligand 2,2’-bipyridine substituted IP T by a semicarbazone 2-formylopyridine moiety (bpySC: 5-(4-{4'-methyl-[2,2'-bipyridine]-4- CR yl}but-1-yn-1-yl)pyridine-2-carbaldehyde semicarbazone) and as the others 2,2’-bipyridine (bpy) and 4,7-diphenyl-1,10-phenanthroline (dip), respectively, as auxiliary ligands have been US prepared. Their biological activity has been studied on murine colon carcinoma (CT26) and human lung adenocarcinoma (A549) cell lines. The anti-proliferative activity was dependent on AN the presence of bpy or dip in the complex, with one order of magnitude higher cytotoxicity for M Ru2 (dip ligands). Ru1 (bpy ligands) exhibited a distinct increase in cytotoxicity going from 24 to 72 h of incubation with cells as was not observed for Ru2. Even though both studied ED compounds were powerful apoptosis inducing agents, the mechanism of their action was entirely PT different. Ru1-incubated A549 cells showed a notable increase in cells number in the S-phase of the cell cycle, with concomitant decrease in the G2/M phase, while Ru2 promoted a cell CE accumulation in the G0/G1 phase. In contrast, Ru1 induced marginal oxidative stress in A549 AC cell lines even upon increasing the incubation time. Even though Ru1 preferably accumulated in lysosomes it triggered the apoptotic cellular death via an intrinsic mitochondrial pathway. Ru1incubated A549 cells showed swelling and enlarging of the mitochondria. It was not observed in case of Ru2 for which mitochondria and endoplasmic reticulum were found as primarily localization site. Despite this the apoptosis induced by Ru2 was caspase-independent. All these findings point to a pronounced role of auxiliary ligands in tuning the mode of biological activity. 2 ACCEPTED MANUSCRIPT 1. Introduction One of the most important issues in the field of medicinal inorganic chemistry concerns the discovery of more effective and safer anticancer drugs. Many of the currently studied metallodrugs are designed to be prodrugs and selectively activated in the cancer tissue. However, T a major advantage of this strategy can also be its main weakness, since several possible active IP molecules are produced and start to interact with biomolecules in the human body. Investigation CR of all these interactions is very challenging and is still the focus of many studies. Because of this, US the perspective about designing new anti-cancer drugs slowly shifted [1], and an increased attention is paid to ruthenium compounds inert to substitution mainly those with polypyridyl ligands. AN Their electronic and structural properties can be tuned easily by the selection of appropriate ligands giving rise to the formation of versatile compounds which might be designed either for therapeutic ED M and/or optical imaging purpose. The design of potential drugs based on organic compounds usually involves the modification of the PT lead structure in respect to the site of action, or otherwise new compounds are formed based on the CE known molecular targets (e.g. receptor proteins or enzymes) [2]. Even though many active rutheniumbased compounds have been discovered, their biological activity mechanism remains unclear and AC their targets still unidentified. The lack of this knowledge hampers rational design of new anticancer agents based on these complexes. A new approach recently developed, is to design compounds where one or more polypyridyl ligands around ruthenium center are modified by anchoring an organic molecule with a known biological target or mechanism of action. The choice of the organic targeting molecule is critical since it can have various functions such as i) tuning the lipophilic character of the whole Ru complex for specific subcellular accumulation (mitochondria, reticulum endoplasmic, nucleus, lysosome) [3, 4]; ii) targeting the specific 3 ACCEPTED MANUSCRIPT receptors, enzymes or cellular processes [5, 6]; iii) oxygen-dependent accumulation in cells [7, 8]; iv) creating synergistic effects between the biologically active ligand systems and the metal centre; v) tuning the photophysical/photochemical properties for an appropriate light activation (photodynamic and photoactivated therapy) [9, 10]; vi) combining therapy and diagnosis IP T (theranostics) [11] and others. CR In this context, we have designed two new ruthenium(II) polypyridyl complexes in which one bipyridyl ligand is modified by a semicarbazone 2-formylopyridine (Scheme 1). α-N-heterocyclic US (thio)semicarbazones and their metal complexes are known as anticancer agents [12-14] therefore AN combining such moiety with Ru(II) polypyridyl complexes might bring additional benefits towards their anticancer activity. The chosen semicarbazone is a structural analogue of 3- M aminopyridine-2-carboxyaldehyde thiosemicarbazone, which is currently clinically tested as an ED anticancer drug (Triapine®) [15, 16]. The anticancer activity of the Triapine® arises from its ability to inhibit the action of ribonucleotide reductase (RR) [17]. The catalytically active centre PT of RR comprises a tyrosyl radical stabilized with two iron ions which might be a target for CE Triapine® having good metal chelating properties [18]. Ribonucleotide reductase is required for DNA synthesis since it catalyses the reduction of ribonucleotides into deoxyribonucleotides. AC Consequently the inhibition of this enzyme interrupts cell proliferation. To take an advantage of its chelating properties, semicarbazone 2-formylopyridine moiety was kept away from Ru centre by a spacer based on an alkyne chain (Scheme 1). 2,2’-bipyridine (bpy) and 4,7-diphenyl-1,10phenanthroline (dip) were chosen as auxiliary ligands to evaluate the impact of their diverse lipophilic character and size on the biological activity. The synthesis, photophysical properties and biological evaluation on two cancer cell lines: murine colon carcinoma (CT26) and human lung adenocarcinoma (A549) of the Ru1 and Ru2 complexes are reported. Their cytotoxicity, 4 ACCEPTED MANUSCRIPT cellular distribution, induction of apoptosis, effect on cell-cycles, mitochondria potential, intracellular calcium concentration as well as reactive oxygen production (ROS) are discussed in relation to the parent ruthenium(II) complexes ([Ru(bpy)3]2+ and [Ru(dip)2(bpy)]2+) to understand their mechanism of action. Our results prove that the choice of the auxiliary ligands might have a T predominate effect on the mode of action of ruthenium complexes having one ligand modified Me N N US CR IP with biologically active organic substituent. 2+ AN Ru N N Me N N N N N N N N O N NH2 Ru2 ED Ru1 N H N 2+ Ru M O N N N H NH2 CE PT Scheme 1. Ruthenium compounds studied in this work. 2. Materials and methods AC 2.1. Synthetic procedures All solvents were at analytical grade and were used without further purification. DMF was stirred over calcium hydride for 12 h, filtrated and distilled from over potassium carbonate [19]. Diisopropylamine was distilled over NaH and stored under argon [19]. Reagents were purchased from Sigma-Aldrich (ruthenium(III) chloride, n-butyllithium solution in hexanes, isopropylmagnesium solution in THF, 2,2’-bipyridyl, 4,7-diphenyl-1,10-phenantroline), Alfa 5 ACCEPTED MANUSCRIPT aesar (5-bromo-2-iodopyridine, semicarbazide hydrochloride, 3-(trimethylsilyl)propagyl bromide) concentration of n-butyllithium solution was determined by titration of diphenylacetic acid in dry THF [20]. T 2.1.1. Synthesis of 4-(3-(trimethylsilyl)prop-2-yn-1-yl)-4’-methyl-2,2’-bipyridyl (2). To a IP solution of freshly distilled diisopropylamine (0.19 mL, 1.3 mmol) in anhydrous THF (5 mL) CR under argon conditions at -78°C, a solution of n-butyllithium in hexane (0.75 mL, 1.2 mmol) was added dropwise. The solution was stirred for 30 minutes at -78°C and then warmed up to 0°C. A US solution of 4,4’-dimethyl-2,2’-bipyridine (1) (0.184 g, 1 mmol) in dry THF (10 mL) was then AN added. After 2 h, 3-(trimethylsilyl)propagyl bromide (0.25 mL, 1.5 mmol) was added rapidly. After another hour, the mixture was warmed to room temperature and quenched with water (30 M mL). The organic phase was extracted with diethyl ether (3x20 mL) and the combined organic ED layers were washed twice with brine and dried over magnesium sulphate. The solvent was removed under reduced pressure to give the pure product 2 (0.276 g, 92%). 2 was found too PT instable to be stored and was involved immediately in the next stage of the synthesis. 1H NMR CE (400 MHz, CDCl3): : 0.11 (s, 9H), 2.44 (s, 3H), 2.58 (t, J=7.2Hz, 2H), 2.91 (t, J=7.2 Hz, 2H), 7.12-7.14 (m, 1H), 7.18 (dd, J=4.8 and 1.6 Hz, 1H), 8.22 (s, 1H), 8.28 (s, 1H), 8.52 (d, J=5.2 Hz, AC 1H), 8.58 (d, J=4.8 Hz, 1H) ppm (Fig. S4). 13C NMR (100 MHz, CDCl3): (ppm): -0.01, 21.05, 21.19, 34.40, 86.16, 105.52, 121.40, 121.98, 124.03, 124.68, 148.11, 148.95, 148.99, 150.34, 155.94, 156.27 ppm (Fig. S5). 2.1.2. Synthesis of 4-(prop-2-yn-1-yl)-4’-methyl-2,2’-bipyridyl (3). To a solution of 2 (0.276 g, 0.9 mmol) in methanol (5 mL) was added potassium carbonate (0.205 g, 1.5 mmol). The mixture 6 ACCEPTED MANUSCRIPT was heated under argon at 50ºC for 2 h. After this time, the reaction was cooled down to 0°C, neutralized with 2M HCl and extracted with diethyl ether (3x30 mL). The combined organic layers were washed twice with brine and dried over magnesium sulphate. The solvent was removed under reduced pressure to give the pure product as a brown solid (0.150 g, 72%). 1H T NMR (400 MHz, CDCl3): d 1.99 (t, J = 2.6 Hz, 1H), 2.44 (s, 3H), 2.54 (td, J =7.4 and 2.6 Hz, IP 2H), 2.94 (t, J = 7.4 Hz, 2H), 7.13 (d, J=4.8 Hz, 1H), 7.20 (dd, J =5.0 and 1.8 Hz, 1H), 8.23 (d, , CR J =0.8 Hz, 1H), 8.26 (d, J =0.8 Hz, 1H), 8.52 (d, J=5Hz, 1H), 8.58 (d, J=5Hz, 1H) ppm (Fig. S6). 13 C NMR (100 MHz, CDCl3): d 20.41, 21.12, 34.50, 68.87, 83.79, 120.71, 121.63, 124.04, US 125.02, 147.99, 148.33, 148.90, 151.03, 155.89, 156.32 ppm. [HRMS – ESI] Calculated for AN C15H14N2 m/z : 223.1230 (M+H+), Found: m/z = 223.1239 (M+H+). M 2.1.3. Synthesis of 5-bromo-2-formylpyridine (5) [21]. 5-bromo-2-formylpyridine was ED synthesized modifying the procedure described by Song et al. [21]. To a solution of 5-bromo-2iodopyridine (4) (0.586 g, 2 mmol) in anhydrous THF (10 mL) under argon conditions at -10°C, PT a solution of isopropylmagnesium chloride (1.5 mL, 2.17 mmol) was added dropwise. After 2 h, CE dry DMF (0.4 mL, 5.16 mmol) was added rapidly. The mixture was kept at -10°C for another hour and then warmed up to room temperature over 2 h. The reaction was quenched with a AC saturated aqueous solution of NH4Cl (20 mL) and extracted with diethyl ether (3x25 mL). The combined organic layers were washed twice with brine and dried over magnesium sulphate. The solvent was removed under reduced pressure to give pure product as light yellow solid (0.306 g, 80%). 1H NMR (200 MHz, CDCl3):  7.84 (dd, J = 8.2 and 0.8 Hz, 1H), 8.02 (ddd, J = 8.2, 2.2 and 0.8 Hz, 1H), 8.85 (d, J=2 Hz, 1H), 10.04 (d, J=0.8 Hz, 1H) ppm. 7 ACCEPTED MANUSCRIPT 2.1.4. Synthesis of 2-[(5-bromopyridin-2-yl)methylidene]hydrazinecarboxamide (6). To a suspension of semicarbazide hydrochloride (0.149 g, 1.3 mmol) in anhydrous ethanol (3 mL), a solution of 5 (0.230 g, 1.2 mmol) in ethanol (9 mL) was added. The mixture was refluxed over 3 h and cooled down to 0°C. The solid was filtrated, washed twice with cold, anhydrous ethanol, T once with diethyl ether and dried in vacuum to give the pure product as light cream powder IP (0.300 g, 99%). 1H NMR (400MHz, DMSO-d6)  7.02 (brs, 2H), 7.86 (s, 1H), 8.10 (dd, J = 8.0 CR and 1.6 Hz, 1H), 8.15 (d, J = 8.0 Hz, 1H), 8.67 (d, J = 1.6 Hz, 1H), 10.63 (s, 1H) ppm (Fig. S7). 13 CNMR (100MHz, DMSO-d6): 119.70, 121.57, 137.78, 139.73, 149.26, 152.25, 156.29 ppm US (Fig. S8). [HRMS-ESI]: Calculated for C7H7N4OBr: m/z 264.9701 (M+Na+) Found 264.9692 Synthesis of 5-(4-{4'-methyl-[2,2'-bipyridine]-4-yl}but-1-yn-1-yl)pyridine-2- M 2.1.5. AN (M+Na+). ED carbaldehyde semicarbazone (bpySC). To a solution of 3 (0.170 g, 0.75 mmol) in acetonitrile (6 mL), copper (I) iodide (0.05 g, 30 mol%) and Tetrakis(triphenylphosphine)palladium(0) (0.045 PT g, 5 mol%) were added under argon conditions. Diisopropylamine (6 mL) was added and the CE mixture was stirred for 15 min. After that, a suspension of 6 (0.210 g, 0.9 mmol) in methanol (1 mL) was added. The mixture was refluxed for 18 hours. Concentrated ammonia (1 mL) was AC added to the brown suspension and the mixture was filtrated through Celite (followed by 70 mL of acetonitrile). The solvent was removed under reduced pressure and the residue was dissolved in dichloromethane/concentrated ammonia mixture. The organic phase was separated, washed twice with concentrated ammonia (till all copper was removed), once with brine and dried over magnesium sulfate. The solvent was removed under reduced pressure to give the crude product which was dissolved in chloroform (15 mL) and treated with cyclohexane (60 mL). The mixture 8 ACCEPTED MANUSCRIPT was kept at 4°C (fridge) and crystals were filtrated, washed with cyclohexane and dried under vacuum to give the pure product as a white solid (0.132 g, 45%). 1H NMR (600 MHz, CDCl3): d 2.45 (s, 3H), 2.84 (t, J =7 Hz, 2H), 3.03 (t, J = 7 Hz, 2H), 7.14 (dd, J =16.2 and 4.8 Hz, 2H), 7.64-7.77 (m, 3H), 8.25 (s, 1H), 8.38 (s, 2H), 8.53-8.63 (m, 3H) ppm (Fig. S9). 13C NMR (150 T MHz, CDCl3) d 20.67, 21.22, 34.17, 78.86, 93.77, 119.41, 120.83, 121.33, 122.04, 123.89, IP 124.83, 138.90, 141.49, 148.23, 148.95, 149.18, 150.04, 151.14, 152.11, 155.79, 156.38, 156.79 CR ppm (Fig. S10). [HRMS-ESI]: Calculated for C22H20N6O m/z 385.1771 (M+H+) Found 385.1771 US m/z (M+H+). AN 2.1.6. General procedure for synthesis of cis-Ru(NN)2Cl2. Ruthenium(III) chloride trihydrate (0.262 g, 1 mmol), the ligand (2,2’-bipyridine or 4,7-diphenyl-1,10-phenantroline) (2 mmol) and M 2 drops of N-ethylmorpholine were dissolved in degassed N,N-dimethylformamide (10 mL) ED under argon conditions. The mixture was put into a microwave reactor for 30 min (250W, 160ºC). The solvent was then removed under reduced pressure to c.a. 1 mL and acetone (20 mL) PT was added. After 24h at -20ºC, the dark solid obtained was filtrated and washed with cold CE acetone, twice with diethyl ether and dried under vacuum. The crude product was finally purified product. AC by flash chromatography (neutral Al2O3, dichloromethane/methanol (5/95)) to give the pure 2.1.6. 1. cis-Ru(bpy)2Cl2 (8) [22]. 8 was obtained using 2,2'-bipyridine as ligand (0.181 g, 38%). 1 H NMR (200 MHz, DMSO-d6):  7.11 (t, J =8Hz, 2H), 7.51 (d, J=5.2Hz, 2H), 7.69 (t, 2H, J=8Hz), 7.78 (t, J =7Hz, 2H), 8.08 (t, J =8Hz, 2H), 8.48 (d, J =8Hz, 2H), 8.64 (d, J =8Hz, 2H), 9.97 (d, J=5Hz, 2H) ppm. [HRMS-ESI]: Calculated for C20H16N4RuCl2: m/z 483.9784 m/z (M+) Found 483.9791 (M+). 9 ACCEPTED MANUSCRIPT 2.1.6.2. cis-Ru(dip)2Cl2 (9) [23]. 9 was obtained using 4,7-diphenyl-1,10-phenantroline as ligand (0.460 g, 55%). 1H NMR (600 MHz, DMSO-d6):  7.45-7.65 (m, 2H), 7.70 (t, J =7.8Hz, 4H), 7.81 (d, J =7.2Hz, 4H), 7.97 (d, J =9Hz, 2H), 8.25 (s, 1H), 8.27 (s, 1H) ppm. [HRMS-ESI]: Calculated for C48H32N4RuCl2: m/z 859.0929 m/z (M+Na+) Found 859.0949 (M+Na+). T 2.1.6.3. Synthesis of [Ru(bpy)2(bpySC)]Cl2 (Ru1). bpySC (0.023 g, 0.060 mmol) was IP dissolved in absolute ethanol (5 mL) under argon conditions. A solution of cis-Ru(bpy)2Cl2(8) CR (0.023 g, 0.048 mmol) in absolute ethanol (5 mL) was finally added. The dark violet mixture was refluxed under argon for 16 h. After that, the solvent was removed under reduced pressure the US residue was dissolved in water (1 mL) and filtrated. The pure product was obtained after AN crystallization from water as dark red crystals (0.033 g, 80%). 1H NMR (600 MHz, CD3CN):  2.51 (s, 3H), 2.91 (t, J=6 Hz, 2H), 2.95 (t, J=6 Hz, 2H), 7.19 (s, 1H), 7.33-7.40 (m, 6H), 7.46 (d, M J=7.8 Hz, 1H), 7.51 (d, J=6 Hz, 1H), 7.61 (d, J=6 Hz, 1H), 7.71-7.74 (m, 6H), 7.80 (t, J=7.8 Hz, ED 1H), 8.03-8.07 (m, 4H), 8.13 (s, 1H), 8.25 (d, J=6 Hz, 1H), 8.54-8.66 (m, 8H) ppm (Fig. S11). [HRMS] Calculated for C42H36N10ORu: m/z 399.1052 (M+), Found 399.1058, (M+) Anal. Calc. PT for C42H36N10ORu: C (58.1%), H (4.2%), N (16.1%), Found: C (58.2%), H (4.4%), N (16.1%). CE 2.1.6. 4. Synthesis of [Ru(dip)2(bpySC)]Cl2 (Ru2). To a solution of 9 (0.019 g, 0.023 mmol) in absolute ethanol (10 mL) under argon conditions, was added a solution of bpySC (0.010 g, 0.026 AC mmol) in absolute ethanol (5 mL). The mixture was refluxed for 22 h. After that time the solvent was removed under reduced pressure. The crude product was dissolved in dichloromethane and purified by flash chromatography (Al2O3 neutral, dichloromethane/Methanol(5/95 to 10/90 gradient) to give the pure product with yield (0.013 g, 47%). 1H NMR (600 MHz, CD3CN)  2.55 (s, 3H), 2.95 (t, J =6 Hz, 2H), 3.13 (t, J=6 Hz, 2H), 7.04 (s, 1H), 7.22 (d, J=6 Hz, 1H), 7.37 (dd, J=15.6 Hz, 6 Hz, 2H), 7.57-7.63 (m, 20H), 7.67 (d, J=5.4 Hz, 2H), 7.73 (dd, J=5.4 and 2.4 Hz, 10 ACCEPTED MANUSCRIPT 2H), 7.79 (t, J=5.4 Hz, 1H), 8.13-8.20 (m, 6H), 8.23 (d, J=5.4 Hz, 1H), 8.26 (d, J=5.4 Hz, 1H), 8.33 (d, J=5.4 and 3.6 Hz, 1H), 8.80 (d, J=12.6 Hz, 1H), 8.90 (d, J=12.6 Hz, 1H) ppm (Fig. S12). [HRMS]: m/z: Calculated for C70H52N10ORu: m/z 575.1679 (M+), Found 575.1658 (M+). T 2.2. Spectroscopy measurements IP UV-Vis absorption spectra of ruthenium complexes were recorded at 25ºC in water using Perkin CR Elmer Lambda 35 spectrophotometer. Luminescence measurements were registered on Perkin Elmer LS55 spectrofluorimeter in the range 480 - 900 nm upon excitation at the maximum of US charge transfer band for each ruthenium complex. The average of three scans was subjected to AN smoothing. For the determination of the quantum yield of luminescence (Φ), aqueous solutions of [Ru(bpy)3]2+ with a small amount of DMSO (<0.008% v/v) were used as standards (Φ = 0.028 M [24] and 0.042 [25] for air-equilibrated and deoxygenated conditions, respectively). The spectra ED for the ruthenium complexes were recorded at a concentration that had an absorbance less than following equation:[26] PT 0.05 units at the excitation wavelength. The quantum yield was calculated according to the CE Φ = Φref × [Aref/A] × [I/Iref] × [n2/nref2] where I is the integrated luminescence intensity, A is the optical density, and n is the refractive AC index, ref refers to the values for the reference. The mean value was calculated from a minimum of three independent experiments. Luminescence lifetime experiments were performed at room temperature using Fluorolog-3 Horiba Jobin Yvon with single photon counting technique. The excitation wavelength was fixed at 464 nm (NanoLED diode) and average luminescence lifetime was measured at emission maximum. The instrument response functions were measured using a light scattering solution of Ludox (colloidal silica, Sigma-Aldrich). The DAS6 software (HORIBA Scientific) was used for 11 ACCEPTED MANUSCRIPT deconvolution of the obtained decays and for calculation of the lifetime values. Two or three exponential fit were chosen based on χ2 parameter (the goodness of fit evaluation). A singleexponential fit was found to be an optimal description of the obtained results for the ruthenium T compounds. IP 2.3. Computational characterization CR To obtain ground state geometries and electronic structures of Ru1 and Ru2 Density Functional Theory (DFT) was applied using hybrid B3LYP functional [27-31] and 6-31G(d,p) basis set [32- US 35] for all atoms except for ruthenium, for which LANL2DZ basis-set [36, 37] was applied. To AN compute electronic excitation spectra, Time Dependent – Density Functional Theory (TD-DFT) was used with the same functional and basis sets for light atoms, with LANL2DZ pseudo- M potential for Ru. Eighty lowest laying electronic excitations were determined. All calculations ED were done with Gaussian 09 program [38], orbitals were visualized using GaussView [39] PT software. CE 2.4. Cell Culture Conditions Biological studies were performed using murine colon carcinoma CT26 and human lung AC adenocarcinoma A549 cell lines. Cells were maintained in DMEM medium supplemented with 10% fetal bovine serum (FBS) and 1% antibiotics – penicillin (100 units/mL) and streptomycin (100 μg/mL). Cells were routinely cultured at 37 °C in a humidified incubator in a 5% CO2 atmosphere. 2.5. Cytotoxicity 12 ACCEPTED MANUSCRIPT The evaluation of the cytotoxicity of the Ru complexes on A549 and CT26 cells, was conducted using an Alamar Blue assay. The Alamar Blue test is based on the reduction of blue and nonfluorescent subtrate (resazurin) to a pink and highly fluorescent product (resorufin) by the alive cells. Cells were seeded on a 96 wells plate with a density of 1.5 × 10 4 cells per cm2 one day T before the experiments. Then, cells were incubated with various concentrations of the Ru IP compounds and synthesized ligand L1 for 24/72 hours in the dark. All compounds were diluted in CR DMSO and then, added to the appropriate medium with or without 2% FBS to obtain the applied concentrations. The final DMSO concentration was kept constant at 0.1% (v/v) in case of Ru2 US and 0.5% (v/v) in case of Ru1 and bpySC. After the incubation, cells were washed with PBS and AN incubated in the resazurin sodium salt solution (25 µM) for 3 h. The cell viability was quantified at 605 nm using 560 nm excitation light (Tecan Infinite 200 microplate reader). Experiments M were performed in triplicate and repeated at least three times to get the mean values ± standard ED deviation. The viability was calculated with respect to the untreated cells control. The IC50 values PT were determined using the Hill equation (Origin 9.0) [40] (𝑦100 − 𝑦0 )[𝑐]𝐻 [𝐼𝐶50 ]𝐻 + [𝑐]𝐻 CE y = y0 + AC 2.6. Cellular imaging of accumulated Ru complexes For co-localization experiments, A549 cells were seeded on a 6 well plate at a density of 3 × 104 cells per cm2 24 h prior to the staining. ER-Trackert Blue-White DPX, Mitotracker Green and Lyso-Tracker Blue (Life Technologies) were used to image ER, mitochondria and lysosomes according to the manufacturer’s protocols. The Ru complexes were incubated in basic medium for 24 h ([Ru1] = 500 µM, [Ru2] = 2 µM), then rinsed twice with PBS. The chosen concentration of the Ru complexes was not cytotoxic to the cells under these conditions. Images were acquired 13 ACCEPTED MANUSCRIPT using a Olympus fluorescence microscope IX51 equipped with an XC10 camera with 470–495 and 530–550 nm emission filters. 2.7. Cell cycle T A549 cells were seeded into a 6 wells plate with a density of 3 × 104 cells per cm2. Cells were IP cultured in the full medium for 1 day. Then, the medium was removed and replaced with a basic CR medium containing various concentrations of the studied compounds, and incubated for 24 h. Then, the cells were washed with PBS, detached by trypsin, fixed in cold methanol for 30 min, US stained with propidium iodide (PI) for 4 h in the dark, followed by analyzing using a BD AN LSRFortessa cytometer. The experiment was performed twice. M 2.8. Apoptosis ED The early stage of apoptosis is manifested by the relocation of phosphatidylserine (PS) from the inner side of the cellular membrane to the outer side. This process can be revealed by the staining PT cells with the labeled Annexin V. Annexin V is a cellular protein that in the presence of Ca2+ CE ions, selectively binds to PS. DAPI was used instead of propidium iodide to assess the cell necrosis, due to the overlapping excitation/emission parameter of the propidium iodide and the AC Ru complexes in live cells [41]. A549 cells were seeded into a 6 wells plate with a density of 3 × 104 cells per cm2 and cultured in the full medium for 1 day. Afterwards, the medium was removed and replaced by a medium containing different amounts of the studied compounds and incubated for 24 h. Then, cells were washed with PBS and binding buffer. The cells were stained with Annexin V-FITC for 10 min in the dark and then, with DAPI (0.5 µM) for 5 min. Cells were analyzed by a BD LSRFortessa cytometer. As a positive control, H2O2 (300 µM) was used. 14 ACCEPTED MANUSCRIPT 2.9. Caspases activity Activation of caspases 3/7, 8 and 9 was examined using luminescent Caspase Glo assays (Promega) according to the manufacturer’s manual. A549 and CT26 cells were seeded on a white 96 wells plate with a density of 1.6 × 104 cells per cm2 24 h prior to the experiments. Next, the T compounds at different concentrations were added to the wells and incubated for 24 h ([Ru1] = IP 200 µM, [Ru2] = 2 µM, [bpySC] = 100 µM). The luminescence intensity of the cells was CR measured using a Tecan Infinite 200 plate reader. US 2.10. Mitochondrial morphology AN MitoTracker Green (ThermoFisher Scientific) was used to visualize mitochondria of A549 cells. A549 cells were seeded on a 6 wells plate with a density of 3 × 104 cells per cm2 24 h prior to the M experiments. Next, the Ru complexes were added and incubated for 24 h. After the incubation, ED the Ru compounds were washed and cells were stained with MitoTracker Green (100 nM) for 30 min at 37 °C. After the staining, cells were visualized using an Olympus fluorescence microscope CE PT IX51. 2.11. Cytosolic calcium homeostasis AC Cytosolic calcium concentration was measured using Fluo-8 AM probe (AAT Bioquest). A549 and CT26 cells were seeded on a 96 wells plate with a density of 1.5 × 104 cells per cm2 one day before the experiments. Then, cells were incubated with various concentrations of the compounds for 24 h in the dark. Next, cells were washed with PBS and stained with Fluo-8 AM (4 µM) for 30 min in the dark at 37 °C. After staining cells were washed twice with PBS and analyzed by a Tecan Infinite 200 microplate reader measuring fluorescence of the probe at 525 nm using 490 15 ACCEPTED MANUSCRIPT nm as an excitation wavelength. Experiment was performed three times in triplicate and the mean values ± standard deviations were calculated. 2.12. Mitochondria membrane potential T Mitochondria membrane potential was evaluated using JC-1 probe (AAT Bioquest). A549 and IP CT26 cells were seeded on 96 wells plate with a density of 1.5 × 104 cells per cm2 one day before CR the experiments. Cells were incubated with various concentrations of the Ru compounds for 24 h in the dark. Then, cells were washed with PBS and stained with JC-1 (10 µM) for 30 min in the US dark at 37 °C. Next, cells were washed with PBS and analyzed by a Tecan Infinite 200 AN microplate reader measuring fluorescence of the probe at 525 nm and 590 nm using 490 nm as an 2.13. Total ROS production ED standard deviations were calculated. M excitation wavelength. Experiment was performed three times in triplicate and the mean values ± PT The level of the oxidative stress induced in cells after the incubation with the Ru complexes was CE conducted for A549 and CT26 cell lines using the cyto-ID Hypoxia/Oxidative stress detection kit. A549 and CT26 cells were seeded with a density of 3 × 104 cells per cm2, respectively. A day AC later the compounds at different concentrations in medium without serum were added and incubated in the dark for 24/72 h. Then, cells were washed with PBS, treated with trypsin and analyzed by BD LSR cytometer. As a positive control, pyocyanin (300 µM) was used. The level of the oxidative stress was determined as a percentage of the ROS positive cells of the whole cell population. 16 ACCEPTED MANUSCRIPT 3. Results and discussion 3.1 Synthesis T The preparation of the target complexes Ru1 and Ru2 required the synthesis of ligand bpySC IP (Scheme 2) that was synthesised by a Sonogashira coupling between 4-(but-3-yn-1-yl)-4'-methyl- CR 2,2'-bipyridine (3) and 5-bromopyridine-2-carbaldehyde semicarbazone (6). 6 was synthesised by US formylation of 5-bromo-2-iodopyridinefollowed by treatment with semicarbazide hydrochloride. 3 was synthesised by a selective monolithiation of 4,4’-dimethyl-2,2’-bipyridine (1) using LDA AN followed by reaction with 3-(trimethylsilyl)propagyl bromide and final deprotection using M potassium bicarbonate [21]. ED Me Me TMS Me Me N N Br CE 1 PT (a) N (c) N N 3 Br (d) Br N O N CHO 5 AC 4 N 2 N I (b) N N H NH2 6 Me (e) O N NH2 3+6 N N N NH bpySC 17 ACCEPTED MANUSCRIPT Scheme 2. Synthesis of ligand bpySC Reagents and conditions: (a) (1) LDA, -78ºC, THF, 0.5h then 0ºC, 2h; (3) 3-(trimethylsilyl)propagyl bromide, 1h; (b) K2CO3, MeOH, 50ºC, 2h; (c) (1) iPrMgCl, -10ºC, THF, 2h; (2) DMF, -10ºC -> RT 2h; (d) NH2-NH-C(=O)-NH2·HCl, EtOH, T reflux, 3h; (e) CH3CN, CuI, Pd(PPh3)4, diisopropylamine, reflux, 18h. IP Complexes Ru1 and Ru2 were synthesised by refluxing cis-Ru(NN)2Cl2 complexes and bpySC CR in absolute ethanol. Dichlorobis(2,2'-bipyridine)ruthenium(II) (Ru(bpy)2Cl2) and dichlorobis(4,7diphenyl-1,10-phenantroline)ruthenium(II) (Ru(dip)2Cl2) were used for Ru1 and Ru2, US respectively. The cis-Ru(NN)2Cl2 complexes were prepared by microwave synthesis from AN ruthenium(III) chloride and the proper ligand in DMF according to previously described procedures [42, 43]. Interestingly, the coordination of ruthenium occurred exclusively on the M bipyridine side of the bpySC and no trace of ruthenium coordination by the SC moiety was 8, L=bpy 9, L=dip EtOH, Ar, reflux, 22h Ru1, L=bpy Ru2, L=dip PT bpySC L2RuCl2 ED observed. AC CE Scheme 3. Synthesis of Ru1 and Ru2. 3.2. Photophysical properties The complexes have been characterized by UV-Vis spectroscopy using water as solvent. The photophysical data are collected in Table 1. In order to measure the effect of bpySC on the properties, complexes containing one bpy instead of bpySC were prepared and characterized. As shown in Table 1 all complexes displayed intense 1MLCT (metal ligand charge transfer) bands in the visible part of the spectrum, around 450 nm. Both Ru1 and Ru2 showed a slight red shift 18 ACCEPTED MANUSCRIPT compared with their unsubstituted counterparts. In contrast, the emission band exhibited a notable blue shift (11 nm for Ru1 and 10 nm for Ru2). The introduction of the bpySC ligand also came with a decrease of the luminescence quantum yield (QY) that were 0.92% and 1.18% for Ru1 and Ru2 respectively under air-equilibrated conditions while argon-equilibrated conditions T allowed to increase these values to 1.63%. and 2.62%, respectively. A decay of the MLCT IP excited state lifetimes was also observed for both Ru1 and Ru2. Thus while globally affecting CR negatively the luminescence of the complexes, the bpySC ligand allowed to maintain QY and AC CE PT ED M AN US lifetimes exploitable for further use in imaging experiments. 19 ACCEPTED MANUSCRIPT Table 1. Photophysical properties of the ruthenium(II) complexes in air-equilibrated and deoxygenated aqueous solutions. (air-equilibrated (deoxygenated conditions) conditions) λmax ε IP λmax Emission T Absorption Emission Φ -1 [M cm ] [nm] τ [µs] Φ CR [nm] -1 438 19 000 461 18 500 286 108 600 15 400 455 18 100 279 CE 427 204 800 435 42 100 Ru2 457 43 000 0.57 ± 0.0420b 0.01 0.01 0.0367 ± 0.76 ± 0.1245 ± 2.51 ± 0.0004 0.01 0.0004 0.01 0.0092 ± 0.27 ± 0.0162 ± 0.36 ± 0.0009 0.03 0.0002 0.06 0.0118 ± 0.65 ± 0.0262 ± 1.72 ± 0.0003 0.03 0.0004 0.07 613 M 88 100 ED 279 AC Ru1 14 000 PT [Ru(dip)2(bpy)]2+ c 452 0.0280a AN 628 US 0.37 ± [Ru(bpy)3]2+ τ [µs] 617 623 data taken from a [24]; b [25];c [44] 3.3. Computational characterization 20 ACCEPTED MANUSCRIPT Quantum chemical calculations within Density Functional Theory (DFT) approach allowed for determination of the Ru1 and Ru2 geometry structures (compare Supplementary Information) and characterization of their frontier orbitals (Fig. S1). In both complexes, HOMO spans over the bpySC ligand, whereas LUMO is delocalised over pyridine atoms of the remaining ligands of T ruthenium: other bpys in Ru1 and bpy fragment of bpySC in Ru2. Further, the performed Time- IP Dependent DFT (TD-DFT) calculations allowed for the characterisation of the spectra of both CR complexes. The most intensive bands clearly show the MLCT character of their visible – see Fig. 1 for schematic representation of their main features. In case of Ru1, the most intensive bands are US centered around 421, 419 and 408 nm, and correspond to excitations from a mixture of Ru d and AN π bpy fragment of bpySC orbitals to π* orbitals of bpy ligands. In case of Ru2, they are present at around 441, 438, 427, 405, and 393 nm, and they might be attributed to the excitations from a AC CE PT ED M mixture of Ru d and π orbitals of dip to π* orbitals of the bpy fragment of bpySC. 21 ACCEPTED MANUSCRIPT AN US CR IP T Ru1 AC CE PT ED M Ru2 Fig. 1. Plots of orbitals responsible for the most intensive absorption bands in the visible range of Ru1 and Ru2 spectra with schematic representation of the most intense absorption bands, as computed with TD-DFT. 22 ACCEPTED MANUSCRIPT 3.4. Cytotoxicity of ruthenium complexes in vitro The cytotoxic effect of the newly synthesised Ru complexes and their reference compounds was determined on two cancer cell lines: murine colon carcinoma (CT26) and human lung T adenocarcinoma cell line (A549). Complexes were tested in serum free conditions (S-) and also IP in the presence of 2% serum (S+). The obtained results are presented in Table 2. Generally, the CR presence of serum reduced the cytotoxic effect of both Ru1 and Ru2. Such an effect has been previously described [45] and might be related to a reduction in the Ru uptake due to binding to US the proteins present in the serum (see Table S1) impeding complexes accumulation. Ru AN complexes with dip ligands were much more cytotoxic in comparison with those having bpy ones. Replacing one of the dip ligands with bpy or bpySC ligand decreases slightly the M cytotoxicity of the Ru compounds. The observed effect arises from the dependence of the Ru ED complexes accumulation and therefore their toxicity on their lipophilicity. In agreement with some previous studies on Ru polypyridyl complexes [44], the poor cellular uptake of PT [Ru(bpy)3]2+ or Ru1 can be related to their weak lipophilic character. CE Increasing the incubation time from 24 to 72 h resulted in a distinct increase in an antiproliferative activity of Ru1, in particular against CT26 cells, while no significant change was AC observed in the cytotoxicity of Ru2. [Ru(bpy)3]2+ remains continuously non cytotoxic even after 72 h of incubation. At the same time a dramatic increase in the toxicity after 72 h was observed for bpySC ligand alone (IC50 ca. 30 times higher). It suggests that this particular ligand might play a crucial role in the anti-proliferative activity of Ru1. Furthermore, it can be assumed that an appropriate selection of auxiliary ligands might lead to a change in action mechanism. For the studied system, switching from two dip ligands to two bpy ones clearly highlighted the cytotoxic 23 ACCEPTED MANUSCRIPT activity of bpySC ligand in Ru1, whereas in Ru2 compound these two auxiliary dip ligands played a key role. Table 2. IC50 of Ru complexes against two cancer cell lines A549 and CT26. Experiments were T performed in medium without (S-) or with (S+, 2%) serum. - 3.3 ± 1.2 2.8 ± 0.8 Ru1 113 ± 154 202 ± 17 97 ± 14 138 ± 20 Ru2 6.8 ± 1.2 9.8 ± 2.3 9.0 ± 1.9 16 ± 2 [Ru(dip)2(bpy)]2+ 4.0 ± 0.7 - - - >320 >320 >320 >320 1.2 ± 0.1 - - - 96 ± 28 - 1.5 ± 0.3 2.0 ± 0.3 201 ± 25 233 ± 38 31 ± 11 50 ± 7.6 Ru2 4.6 ± 0.9 5.0 ± 0.1 5.7 ± 1.5 21 ± 5 [Ru(dip)2(bpy)]2+ 3.4 ± 0.7 - - - [Ru(bpy)3]2+ >320 >320 >320 >320 [Ru(dip)3]2+ 1.2 ± 0.2 - - - US 102 ± 59 CR S+ AN S- bpySC A549 M [Ru(bpy)3]2+ bpySC PT Ru1 ED [Ru(dip)3]2+ AC CT26 S+ CE S- IC50 (µM) 72 h IP IC50 (µM) 24h 3.5. Cell accumulation and cellular targets A549 cells were used to study the accumulation of the studied ruthenium complexes. A higher cellular uptake was found for complex Ru2 in excellent agreement with the cytotoxicity data. 24 ACCEPTED MANUSCRIPT Despite similar luminescence quantum yields for Ru2 and Ru1, much higher concentrations of Ru1 were required to visualize its localization inside the cells. This further confirmed that the accumulation of ruthenium polypyridyl complexes is strongly dependent on their lipophilicity and that in the studied case it is controlled by bpy/dip ligands. Additionally, it points out the T superiority of the accumulation/lipophilicity parameters over luminescence parameters of Ru IP complexes in assessing the potential of the compounds as cellular dyes [44]. CR To further investigate the accumulation of the Ru complexes, organelle-specific dyes were used. Ru2 preferably accumulated into mitochondria and endoplasmic reticulum, as confirmed by US overlapping emission of organelle-specific dyes with the studied Ru complex (Fig. 2). Complex AC CE PT ED M localized within cellular lysosomes (Fig. 3). AN Ru1 exhibited rather small accumulation in those organelles (Fig. S2), while the majority of it is 25 ED M AN US CR IP T ACCEPTED MANUSCRIPT PT Fig. 2. Fluorescence images of A549 cells showing subcellular localization of Ru2 (2 µM, incubation 24 h). (A,C) red colour comes from Ru2 complex emission; (B) ER-Tracker Blue was CE used to image endoplasmic reticulum, blue colour arises from organelle-specific dye while pink AC colour represents overlap of the red luminescence of Ru and blue emission from dye indicating co-localization; (D) MitoTracker Green was used to image mitochondria and green colour arises from organelle-specific dye, while yellow colour represents overlap of the red luminescence of Ru and green emission from dye indicating co-localization. Scale bars 50 µm. 26 CR IP T ACCEPTED MANUSCRIPT US Fig. 3. Fluorescence images of A549 cells showing subcellular localization of Ru1 (500 µM, incubation 24 h). (A) Red colour comes from Ru1 complex emission; (B) LysoTracker Blue was AN used to image lysosomes, pink colour represents overlap of the red luminescence of Ru and blue ED 3.6. Cell-cycle arresting properties M emission from dye indicating co-localization. Scale bars 50 µm. PT The influence of Ru1, Ru2 and bpySC on cell cycle was measured by flow-cytometry (Table 3). The incubation of A549 cells with Ru1 or bpySC induced a significant increase in the number of CE cells in the S-phase of the cell cycle, with the corresponding decrease in the percentage of cells in the G2/M phase. During the S-phase of the cell cycle deoxyribonucleotides, which are DNA AC precursors, are produced. In this phase, corresponding ribonucleotides need to be reduced by ribonucleotide reductase. Inhibition of this enzyme should increase the number of cells arrested in this phase [46, 47]. The S-phase arrest caused by Ru1 or bpySC suggests that their cellular activities might be related to the inhibition of ribonucleotide reductase. Contrarily Ru2 caused increased percentage of the cells in the G0/G1 phase, similarly to other Ru complexes containing 27 ACCEPTED MANUSCRIPT dip ligands [45]. This further confirms the influence of the auxiliary ligands on the biological AC CE PT ED M AN US CR IP T activity of Ru compounds. 28 ACCEPTED MANUSCRIPT Table 3. Cell cycle distribution of A549 cells after 24 h treatment with the Ru polypyridyl Control 57.5% 36.0% 6.5% bpySC 22.2% 74.0% 3.8% Ru1 47.5% 48.4% 4.1% Ru2 76.9% 22.5% 0.6% IP G2/M CR S-phase 3.7. Reactive Oxygen Species (ROS) production US G0/G1 T complexes and with ligand bpySC (representative analysis). AN The influence of Ru1 and Ru2 on reactive oxygen species (ROS) production in cancer cell lines was evaluated. Ru2 as well as the attached ligand bpySC caused significant concentration M dependent increase in ROS production after 24 of h incubation in both A549 and CT26 cell lines ED (Fig. 4, Fig. S3). Increasing the incubation time 24 h to 72 h also increase the ROS level induced by Ru2. However, Ru1 did not induce oxidative stress in the studied cell lines that could be PT partially explained by the lower accumulation of this complex. However increasing the CE incubation time with the compounds from 24 h to 72 h (that will also increase Ru complexes accumulation level) did not induce any increase in ROS production in case of Ru1 as it did with AC Ru2 (Fig. 4). This strongly suggested that the Ru accumulation level is not linked to the lack of ROS production in case of Ru1 and that completely different action mechanism of action responsible for cytotoxic activity depending on whether bpy or dip ligand is present in the ruthenium complex. 29 24 h 72 h 80 60 40 T 20 0 M 50 µ 100 µM 2 µM Ru1 4 µM M 50 µ CR nin trol cya pyo con IP ROS positive cells [%] ACCEPTED MANUSCRIPT µM bpy-SC US Ru2 100 Fig. 4. The level of oxidative stress induced in A549 cells after 24 and 72 h treatment with the Ru AN polypyridyl complexes expressed as percentage of ROS positive cells in the whole cell M population (%). Pyocyanin was used as ROS positive control. ED 3.8. Apoptosis inducing properties PT The determination of the cellular death mechanism was performed using flow cytometry. A549 cells were double stained with Annexin-V- FITC conjugate and DAPI after incubation with Ru1, CE Ru2 and bpySC for 24h. Incubation with all studied compounds significantly increased the AC population of Annexin V-positive cells, indicating cells undergoing early phase of apoptosis (Fig. 5), with no indication of the DAPI-positive cells that would suggest a necrotic cellular death. Despite lesser accumulation of Ru1, that was previously confirmed by the cytotoxicity and localization study, this compound was found to be powerful apoptosis inducing agent. 30 AC CE PT ED M AN US CR IP T ACCEPTED MANUSCRIPT Fig. 5. Apoptosis of A549 cells upon 24 h exposure to the Ru polypyridyl complexes. Cells were labeled with Annexin V-FITC/DAPI. 3.9. Activation of the signalling pathways - caspases activity 31 ACCEPTED MANUSCRIPT Early morphological signs of apoptosis such as translocation of phosphatidylserine are a result of a cascade of biochemical changes occurring within the cell. To further explore the developed changes and investigate the apoptotic mechanism of cellular death of cancer cell lines, caspases activity was measured (Fig. 6). After incubation of A549 and CT26 cells with Ru2, no caspase T activation was observed, indicating that the observed apoptosis occurred via caspase-independent IP pathway. On the contrary, incubation of cells with Ru1 and bpySC induced significant increase CR in activity of initiator caspase 9 and effector caspases 3/7, while no activation of caspase 8 was 8 B 2.0 M 1.5 caspase activity [a.u] AN A ED 1.0 0.5 0.0 control Ru1 PT caspase activity [a.u.] mitochondrial pathway. US detected. This indicates that Ru1 and bpySC triggered apoptotic cellular death via intrinsic Ru2 bpySC 7 6 5 4 3 2 1 0 control Ru1 Ru2 bpySC CE Fig. 6. Caspases 3/7 (black), 8 (red) and 9 (blue) activities after 24 h exposure to the Ru AC polypyridyl complexes and ligand bpySC determined in A549 (A) and CT26 (B) cell lines. This conclusion is further supported by the visualization of the mitochondria of the Ru treated cells (Fig. 7). While no significant change is observed in mitochondria of Ru2 treated cell, incubation of cells with Ru1 caused swelling and enlarging of mitochondria. Such process is often observed in case of apoptotic cell death induced by mitochondria pathway. 32 CR IP T ACCEPTED MANUSCRIPT US Fig. 7. Fluorescence images of A549 cells showing swelling and enlarging of mitochondria after treatment with Ru1. MitoTracker Green was used to image mitochondria and green colour arises AN from a organelle-specific dye (A) untreated cells; (B) cells treated with Ru1 (500 µM) for 24 h. M Scale bars 50 µm. ED 3.10. Mitochondrial membrane potential detection PT Since the studied Ru complexes either accumulated in mitochondria (Ru2) or changed the mitochondria morphology (Ru1), their influence on alteration in mitochondria function was also CE studied by analyzing the mitochondria membrane potential. The loss of the mitochondria membrane potential is often considered to be a prelude to apoptosis. AC The changes of mitochondrial membrane potential induced by the studied complexes were determined using JC-1 mitochondrial probe. At low mitochondrial membrane potential, JC-1 exists in monomeric form and exhibits green fluorescence, but at high mitochondrial membrane potential JC-1 forms aggregates, which exhibit red fluorescence. Two oligopeptides valinomycin and gramicidin were used as positive controls. Valinomycin is K+ ionophore which allows the potassium ions passing freely through the cell membrane and in this way causing the collapse of 33 ACCEPTED MANUSCRIPT mitochondrial membrane potential. Gramicidin is another polypeptide which forms channels in phospholipid membranes and allows ions to pass freely through the membrane leading to the decrease in ΔΨm. The change of mitochondrial potential was represented as change of red/green fluorescence ratio and the results are shown in Fig. 8. All tested compounds caused the decrease T in red/green fluorescence intensity ration, indicating depolarization of mitochondria membrane. IP The effect is stronger in CT26 cells. These results further confirm that Ru1 and bpySC induces CR apoptosis in cancer cells through the mitochondrial signal transduction pathway. US 1.2 A549 CT26 AN 1.0 M 0.8 ED 0.6 PT 0.4 0.2 CE 0.0 control AC red/green fluorescence intensity of JC-1 probe [a.u.] 1.4 50 µM Ru1 100 µM 2 µM 4 µM Ru2 50 µM 100 µM Val Gram bpySC Fig. 8. Effect of the Ru polypyridyl complexes on mitochondrial membrane potential (ΔΨm) in A549 and CT26 cell lines after 24 h treatment measured using JC-1 probe. The results are representative at least three independent experiments. Red fluorescence corresponds to the fluorescence of J-aggregates, while green fluorescence is related to the fluorescence of Jmonomers. The decrease in a ratio of red to green fluorescence values indicates depolarization of 34 ACCEPTED MANUSCRIPT mitochondria membrane potential. Valinomycin (Val) and gramicidin (Gram) were used as positive controls. 3.11. Intracellular calcium concentration T Calcium ion is one of the most important signal transducers in cells, involved in numerous IP physiological and pathological processes. It is known that a variety of metals complexes are able CR to modify intracellular Ca2+ signalling and hence induce apoptosis or necrosis [48, 49]. Using Fluo-8 AM probe the changes in intracellular calcium concentration ([Ca2+]C) in cancer cells after US 24 h incubation with the studied compounds were monitored. The results are presented in Fig. 9. AN Alteration in calcium homeostasis upon treatment with the Ru complexes was cell line dependent. In case of A549 cells, no significant changes in [Ca2+]C after treatment with Ru1 or M bpy-SC were observed. Only Ru2 accumulation caused a decrease in cytosolic calcium level, containing dip ligands [50]. ED and this effect had been already observed previously with other polypyridyl Ru complexes PT Accumulation of Ru1 in CT26 cell line resulted in concentration dependent decrease in CE intracellular calcium level, while Ru2 and bpySC caused the opposite effect - increasing the calcium ions concentration. Such an increase in [Ca2+]C can cause a rise in mitochondrial calcium AC levels since those organelles serves as buffering units and might modulate Ca2+ feedbackinhibition or activation mechanisms. Increase in the mitochondrial calcium concentration can cause the mitochondrial membrane depolarization and lead to higher amounts of reactive oxygen species production. This can force the opening of the mitochondrial permeability pore causing mitochondrial swelling and releasing cytochrome c and other pro-apoptotic factors, initiating programmed cell death process. 35 ACCEPTED MANUSCRIPT 4 6 8 10 600 120 100 80 60 40 20 control 50 µM 100 µM 2 µM Ru1 4 µM 50 µM 100 µM Val 500 400 300 200 100 0 control 50 µM 100 µM 2 µM 4 µM bpy-SC Ru1 Ru2 50 µM 100 µM Val Carb bpy-SC CR Ru2 Carb B IP 0 Fluo-8AM Fluorescence intensity [a.u.] Fluo-8AM Fluorescence intensity [a.u.] 2 A T 0 140 Fig. 9. The effect of the Ru polypyridyl complexes on cytosolic calcium cations concentration US measured with Fluo-8AM in A549 (A) and CT26 (B) cell lines after 24 of incubation. The results are representative for three independent experiments performed in triplicate. Valinomycin (Val) M AN and carbachol (Carb) were used as positive controls. 4. Conclusions ED A new ligand based on semicarbazone 2-formylopyridine moiety conjugated with 2,2’-bipyridyl PT (bpySC) by an alkyne spacer has been developed. The two compounds produced as a result of coordination by ruthenium(II) center by bpySC and either two bpy (Ru1) or two dip (Ru2) CE ligands have been obtained and characterized. They exhibited entirely different biological effects AC on cancer cell lines. The cytotoxic effect determined after 24 h of treatment with Ru2 was more than an order of magnitude higher than that found for Ru1 as well as bpySC ligand alone against both A549 and CT26 cancer cell lines. The extent of treatment up to 72 h resulted in the increased anti-proliferative activity of both Ru1 and bpySC but not of Ru2. The Ru1 complex accumulated preferentially in lysozyme, while Ru2 in mitochondria and endoplasmic reticulum. Both Ru complexes and bpySC induced apoptosis. In the case of Ru2 it occurred via caspaseindependent pathway, while Ru1 and bpySC induced apoptosis in cancer cells through 36 ACCEPTED MANUSCRIPT mitochondria signal transduction pathway, even though this organelle was not the primary localization site. Both studied ruthenium complexes had an opposite effect on intracellular calcium concentration. The increased in ROS production was evident upon treatment with Ru2 while negligible for Ru1 even after prolonged incubation time. T Taken together we have demonstrated that changing of bpy into dip ligands has a strong impact IP on the mechanism of biological activity of the ruthenium(II) complexes. Despite increasing the CR Ru complexes overall accumulation and cytotoxicity by choosing the more lipophilic dip ligands the role of the semicarbazone 2-formylopyridine moiety in biological activity of the ruthenium US complex seems to be marginal. Therefore, a special attention must be paid in choosing AN appropriate auxiliary ligands in designing new ruthenium complexes to take advantage from M conjugation of biologically active molecules to polypyridyl ligands. ED Abbreviations bpy – 2,2’-bipyridine; – semicarbazone; 5-(4-{4'-methyl-[2,2'-bipyridine]-4-yl}but-1-yn-1-yl)pyridine-2-carbaldehyde CE bpySC PT A549 – and human lung adenocarcinoma cell line; AC CT26 – murine colon carcinoma cell line; DAPI – 4',6-diamidino-2-phenylindole; DFT – Density Functional Theory; dip – 4,7-diphenyl-1,10-phenanthroline; DMEM – Dulbecco's Modified Eagle's medium; DMF – dimethylformamide; EtOH – ethanol; 37 ACCEPTED MANUSCRIPT ER – endoplasmic reticulum; ESI – electrospray ionization; FBS – fetal bovine serum; FITC – fluorescein isothiocyanate; T HOMO – highest occupied molecular orbital; IP HRMS – high resolution mass spectrometry; CR IC50 – concentration causing 50 % decrease in viability; iPrMgCl – Isopropylmagnesium chloride; US JC-1 – 5,5,6,6-Tetrachloro-1,1,3,3-tetraethylbenzimidazolylcarbocyanine iodide; AN LDA – lithium diisopropylamide; MeOH – methanol; ED MLCT – metal ligand charge transfer; M LUMO – lowest unoccupied molecular orbital; QY – quantum yield; PT NMR – nuclear magnetic resonance; CE PBS – phosphate buffered saline; PI – propidium iodide; AC ROS – reactive oxygen species; RR – ribonucleotide reductase; S- – in serum free conditions; S+ – in the presence of 2%; THF – tetrahydrofuran; TD-DFT – Time-Dependent DFT. 38 ACCEPTED MANUSCRIPT Acknowledgements The CNRS and French Ministry of Research are thanked for their support. M. Ł. acknowledges the French Embassy in Poland for providing a cotutelle Ph.D. grant. O. M. acknowledges the financial support from the National Science Center (DEC-2013/11/N/ST5/01606). M. B. the financial support from the National Science Center (DEC- T acknowledges IP 2016/21/B/NZ7/01081). This work was carried out using the equipment purchased through CR financial support from the European Regional Development Fund in the framework of the Polish US Innovation Economy Operational Program (contract no. POIG.02.01.00-12-023/08). This AN research was supported in part by PL-Grid Infrastructure. M References [1] A. Bergamo, G. Sava, Dalton Trans. 40 (2011) 7817-7823. ED [2] C. Avendano, J.C. Menendez, Medicinal chemistry of anticancer drugs, Elsevier, 2008. PT [3] L.N. Lameijer, S.L. Hopkins, T.G. Breve, S.H.C. Askes, S. Bonnet, Chem. Eur. J 22 (2016) 18484-18491. CE [4] L. Blackmore, R. Moriarty, C. Dolan, K. Adamson, R.J. Forster, M. Devocelle, T.E. Keyes, AC Chem. 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Sci. 101 (2017) 43-55. 43 M AN US CR IP T ACCEPTED MANUSCRIPT AC CE PT ED Graphical abstract 44 ACCEPTED MANUSCRIPT AC CE PT ED M AN US CR IP T Appropriately chosen auxiliary ligands can regulate not only cytotoxicity and accumulation of polypyridyl ruthenium complexes, but also determine the mechanism of cellular death and highlight the effects of biologically active molecules. 45 ACCEPTED MANUSCRIPT Highlights T IP CR US AN M ED PT CE     New Ru complexes with semicarbazone 2-formylopyridine link to bipyridine were synthesised. As auxiliary ligands bipyridine and diphenylphenanthroline were chosen. The studied compounds were powerful apoptosis inducing agents. The anti-proliferative activity was strongly dependent on auxiliary ligands. The auxiliary ligands determined effect of the complexes on cell cycle arrest and ROS formation. AC  46